{"id":59840,"date":"2016-01-01T18:45:49","date_gmt":"2016-01-01T18:45:49","guid":{"rendered":"https:\/\/leitat.org\/blog\/batcure\/"},"modified":"2025-02-24T20:34:36","modified_gmt":"2025-02-24T20:34:36","slug":"batcure","status":"publish","type":"post","link":"https:\/\/leitat.org\/en\/blog\/batcure\/","title":{"rendered":"BATCURE"},"content":{"rendered":"\t\t<div data-elementor-type=\"wp-post\" data-elementor-id=\"59840\" class=\"elementor elementor-59840 elementor-42431\" data-elementor-post-type=\"post\">\n\t\t\t\t<div class=\"elementor-element elementor-element-c15003c e-flex e-con-boxed e-con e-parent\" data-id=\"c15003c\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t\t<div class=\"e-con-inner\">\n\t\t\t\t<div class=\"elementor-element elementor-element-577d32e elementor-widget elementor-widget-text-editor\" data-id=\"577d32e\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t<div class=\"elementor-widget-container\">\n\t\t\t\t\t\t\t\t\t<ol><li>Developing new therapies for Batten disease<\/li><\/ol><p><a href=\"http:\/\/www.batcure.eu\" target=\"_blank\" rel=\"noopener\">www.batcure.eu<\/a><\/p><p><b>ABSTRACT<\/b><\/p><p>The goal of BATCure is to advance the development of new therapeutic options for a group of rare lysosomal diseases \u2013 neuronal ceroid lipofuscinoses (NCL) or Batten disease. There are &gt; thousand affected across Europe, with a combined incidence of c.1:100 000. The NCLs are devastating and debilitating genetic disorders that mainly affect children, who suffer progressive dementia and motor decline, visual failure and epilepsy, leading to a long period of complete dependence on others, and eventually a premature death. Existing palliative treatment can reduce, but does not eliminate, the burden of seizures and the progressively worsening effects on the whole body due to decreasing CNS influence and control. There are no curative treatments in the clinic for any type of NCL. We will follow a novel integrated strategy to identify specific gene and small molecule treatments for three genetic types of Batten disease that include the most prevalent world-wide, juvenile CLN3 disease, and in southern and Mediterranean Europe, CLN6 and CLN7 diseases.<\/p><p>To develop new therapies for these 3 types of Batten disease, BATCure will:<\/p><ol><li>Create new models, tools and technologies for developing and testing therapies<\/li><li>Further delineate disease biology and gene function to identify new therapeutic target pathways utilising yeast and pluripotent stem cell models<\/li><li>Identify biochemical therapeutic target pathways, facilitate effective evaluation of preclinical therapies and improve diagnostics<\/li><li>Extend a comprehensive natural history beyond the brain to include cardiology, the spinal cord, PNS, psychiatric and metabolic changes<\/li><li>Identify new and repurpose existing small molecule therapy<\/li><li>Triage new compound treatments in zebrafish, a high-throughput small vertebrate model<\/li><li>Deliver and monitor new treatments using mouse models<\/li><li>Provide a novel mechanism to involve patients and their families to inform and fully contribute to therapy development and prepare for clinical trials<\/li><\/ol><p>\u00a0<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<section class=\"elementor-section elementor-top-section elementor-element elementor-element-71d3108 elementor-section-boxed elementor-section-height-default elementor-section-height-default\" data-id=\"71d3108\" data-element_type=\"section\" data-e-type=\"section\">\n\t\t\t\t\t\t<div class=\"elementor-container elementor-column-gap-default\">\n\t\t\t\t\t<div class=\"elementor-column elementor-col-33 elementor-top-column elementor-element elementor-element-4196b17\" data-id=\"4196b17\" data-element_type=\"column\" data-e-type=\"column\">\n\t\t\t<div class=\"elementor-widget-wrap elementor-element-populated\">\n\t\t\t\t\t\t<div class=\"elementor-element elementor-element-a9c2113 elementor-widget elementor-widget-text-editor\" data-id=\"a9c2113\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t<div class=\"elementor-widget-container\">\n\t\t\t\t\t\t\t\t\t<p><strong>Project Budget:<\/strong> 5.995.769 \u20ac<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-0273f3d elementor-widget elementor-widget-text-editor\" data-id=\"0273f3d\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t<div class=\"elementor-widget-container\">\n\t\t\t\t\t\t\t\t\t<p><strong>Leitat Budget:<br \/><\/strong><span style=\"color: var( --e-global-color-text ); font-size: var( --e-global-typography-text-font-size ); font-weight: var( --e-global-typography-text-font-weight ); text-align: var(--text-align);\">213.962 \u20ac<\/span><strong><br \/><\/strong><\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t<\/div>\n\t\t\t\t<div class=\"elementor-column elementor-col-33 elementor-top-column elementor-element elementor-element-5d4d09e\" data-id=\"5d4d09e\" data-element_type=\"column\" data-e-type=\"column\">\n\t\t\t<div class=\"elementor-widget-wrap elementor-element-populated\">\n\t\t\t\t\t\t<div class=\"elementor-element elementor-element-8bd341a elementor-widget elementor-widget-text-editor\" data-id=\"8bd341a\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t<div class=\"elementor-widget-container\">\n\t\t\t\t\t\t\t\t\t<p><strong>Financial Framework: <\/strong>HORIZON 2020<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-05576ba elementor-widget elementor-widget-text-editor\" data-id=\"05576ba\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t<div class=\"elementor-widget-container\">\n\t\t\t\t\t\t\t\t\t<p><strong>Contract number: <\/strong>666918<strong><br \/><\/strong><\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t<\/div>\n\t\t\t\t<div class=\"elementor-column elementor-col-33 elementor-top-column elementor-element elementor-element-7c308fe\" data-id=\"7c308fe\" data-element_type=\"column\" data-e-type=\"column\">\n\t\t\t<div class=\"elementor-widget-wrap elementor-element-populated\">\n\t\t\t\t\t\t<div class=\"elementor-element elementor-element-205798b elementor-widget elementor-widget-text-editor\" data-id=\"205798b\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t<div class=\"elementor-widget-container\">\n\t\t\t\t\t\t\t\t\t<p><strong>Start Date:<\/strong> 01\/01\/2016<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-8b1ff3a elementor-widget elementor-widget-text-editor\" data-id=\"8b1ff3a\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t<div class=\"elementor-widget-container\">\n\t\t\t\t\t\t\t\t\t<p><strong>End Date:<\/strong> 30\/06\/2019<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t<\/section>\n\t\t\t\t<section class=\"elementor-section elementor-top-section elementor-element elementor-element-ba8209d elementor-section-boxed elementor-section-height-default elementor-section-height-default\" data-id=\"ba8209d\" data-element_type=\"section\" data-e-type=\"section\">\n\t\t\t\t\t\t<div class=\"elementor-container elementor-column-gap-default\">\n\t\t\t\t\t<div class=\"elementor-column elementor-col-100 elementor-top-column elementor-element elementor-element-19b638f\" data-id=\"19b638f\" data-element_type=\"column\" data-e-type=\"column\">\n\t\t\t<div class=\"elementor-widget-wrap elementor-element-populated\">\n\t\t\t\t\t\t<div class=\"elementor-element elementor-element-94cd1a6 elementor-widget elementor-widget-text-editor\" data-id=\"94cd1a6\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t<div class=\"elementor-widget-container\">\n\t\t\t\t\t\t\t\t\t<p style=\"text-align: justify;\"><span lang=\"ES\"><b>Partners<\/b><\/span><\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t<\/section>\n\t\t<div class=\"elementor-element elementor-element-353e517 e-flex e-con-boxed e-con e-parent\" data-id=\"353e517\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t\t<div class=\"e-con-inner\">\n\t\t\t\t<div class=\"elementor-element elementor-element-47ab932 elementor-widget elementor-widget-image-gallery\" data-id=\"47ab932\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"image-gallery.default\">\n\t\t\t\t<div class=\"elementor-widget-container\">\n\t\t\t\t\t\t\t<div class=\"elementor-image-gallery\">\n\t\t\t<div id='gallery-1' class='gallery galleryid-59840 gallery-columns-4 gallery-size-full'><figure class='gallery-item'>\n\t\t\t<div class='gallery-icon landscape'>\n\t\t\t\t<img fetchpriority=\"high\" decoding=\"async\" width=\"1280\" height=\"375\" src=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/University_College_London_logo.svg_.png\" class=\"attachment-full size-full\" alt=\"\" srcset=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/University_College_London_logo.svg_.png 1280w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/University_College_London_logo.svg_-300x88.png 300w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/University_College_London_logo.svg_-1024x300.png 1024w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/University_College_London_logo.svg_-768x225.png 768w\" sizes=\"(max-width: 1280px) 100vw, 1280px\" \/>\n\t\t\t<\/div><\/figure><figure class='gallery-item'>\n\t\t\t<div class='gallery-icon landscape'>\n\t\t\t\t<img decoding=\"async\" width=\"351\" height=\"144\" src=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/lios.png\" class=\"attachment-full size-full\" alt=\"\" srcset=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/lios.png 351w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/lios-300x123.png 300w\" sizes=\"(max-width: 351px) 100vw, 351px\" \/>\n\t\t\t<\/div><\/figure><figure class='gallery-item'>\n\t\t\t<div class='gallery-icon landscape'>\n\t\t\t\t<img decoding=\"async\" width=\"200\" height=\"200\" src=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/acureomics.png\" class=\"attachment-full size-full\" alt=\"\" srcset=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/acureomics.png 200w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/acureomics-150x150.png 150w\" sizes=\"(max-width: 200px) 100vw, 200px\" \/>\n\t\t\t<\/div><\/figure><figure class='gallery-item'>\n\t\t\t<div class='gallery-icon landscape'>\n\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"288\" height=\"278\" src=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/university-cardiff.png\" class=\"attachment-full size-full\" alt=\"\" \/>\n\t\t\t<\/div><\/figure><figure class='gallery-item'>\n\t\t\t<div class='gallery-icon landscape'>\n\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"500\" height=\"375\" src=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/Telethon-logo-500x375-1.jpg\" class=\"attachment-full size-full\" alt=\"\" srcset=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/Telethon-logo-500x375-1.jpg 500w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/Telethon-logo-500x375-1-300x225.jpg 300w\" sizes=\"(max-width: 500px) 100vw, 500px\" \/>\n\t\t\t<\/div><\/figure><figure class='gallery-item'>\n\t\t\t<div class='gallery-icon landscape'>\n\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"1280\" height=\"351\" src=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/eppendorf.png\" class=\"attachment-full size-full\" alt=\"\" srcset=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/eppendorf.png 1280w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/eppendorf-300x82.png 300w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/eppendorf-1024x281.png 1024w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/eppendorf-768x211.png 768w\" sizes=\"(max-width: 1280px) 100vw, 1280px\" \/>\n\t\t\t<\/div><\/figure><figure class='gallery-item'>\n\t\t\t<div class='gallery-icon landscape'>\n\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"200\" height=\"200\" src=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/pronexus.png\" class=\"attachment-full size-full\" alt=\"\" srcset=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/pronexus.png 200w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/pronexus-150x150.png 150w\" sizes=\"(max-width: 200px) 100vw, 200px\" \/>\n\t\t\t<\/div><\/figure><figure class='gallery-item'>\n\t\t\t<div class='gallery-icon landscape'>\n\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"1200\" height=\"461\" src=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/mmu.png\" class=\"attachment-full size-full\" alt=\"\" srcset=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/mmu.png 1200w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/mmu-300x115.png 300w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/mmu-1024x393.png 1024w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/mmu-768x295.png 768w\" sizes=\"(max-width: 1200px) 100vw, 1200px\" \/>\n\t\t\t<\/div><\/figure><figure class='gallery-item'>\n\t\t\t<div class='gallery-icon landscape'>\n\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"225\" height=\"224\" src=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/rvc.jpg\" class=\"attachment-full size-full\" alt=\"\" srcset=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/rvc.jpg 225w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/rvc-150x150.jpg 150w\" sizes=\"(max-width: 225px) 100vw, 225px\" \/>\n\t\t\t<\/div><\/figure><figure class='gallery-item'>\n\t\t\t<div class='gallery-icon landscape'>\n\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"630\" height=\"320\" src=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/uni-salamanca.jpg\" class=\"attachment-full size-full\" alt=\"\" srcset=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/uni-salamanca.jpg 630w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/uni-salamanca-300x152.jpg 300w\" sizes=\"(max-width: 630px) 100vw, 630px\" \/>\n\t\t\t<\/div><\/figure><figure class='gallery-item'>\n\t\t\t<div class='gallery-icon landscape'>\n\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"719\" height=\"157\" src=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/orphazyme.png\" class=\"attachment-full size-full\" alt=\"\" srcset=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/orphazyme.png 719w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/orphazyme-300x66.png 300w\" sizes=\"(max-width: 719px) 100vw, 719px\" \/>\n\t\t\t<\/div><\/figure><figure class='gallery-item'>\n\t\t\t<div class='gallery-icon landscape'>\n\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"878\" height=\"584\" src=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/kings-college-logo.jpg\" class=\"attachment-full size-full\" alt=\"\" srcset=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/kings-college-logo.jpg 878w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/kings-college-logo-300x200.jpg 300w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/kings-college-logo-768x511.jpg 768w\" sizes=\"(max-width: 878px) 100vw, 878px\" \/>\n\t\t\t<\/div><\/figure><figure class='gallery-item'>\n\t\t\t<div class='gallery-icon landscape'>\n\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"325\" height=\"155\" src=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/bdf.png\" class=\"attachment-full size-full\" alt=\"\" srcset=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/bdf.png 325w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/bdf-300x143.png 300w\" sizes=\"(max-width: 325px) 100vw, 325px\" \/>\n\t\t\t<\/div><\/figure><figure class='gallery-item'>\n\t\t\t<div class='gallery-icon portrait'>\n\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"400\" height=\"420\" src=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/LEITAT-400x420-1.png\" class=\"attachment-full size-full\" alt=\"\" srcset=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/LEITAT-400x420-1.png 400w, https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/LEITAT-400x420-1-286x300.png 286w\" sizes=\"(max-width: 400px) 100vw, 400px\" \/>\n\t\t\t<\/div><\/figure>\n\t\t<\/div>\n\t\t<\/div>\n\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<section class=\"elementor-section elementor-top-section elementor-element elementor-element-7aef259 elementor-section-boxed elementor-section-height-default elementor-section-height-default\" data-id=\"7aef259\" data-element_type=\"section\" data-e-type=\"section\">\n\t\t\t\t\t\t<div class=\"elementor-container elementor-column-gap-default\">\n\t\t\t\t\t<div class=\"elementor-column elementor-col-100 elementor-top-column elementor-element elementor-element-ea9f40e\" data-id=\"ea9f40e\" data-element_type=\"column\" data-e-type=\"column\">\n\t\t\t<div class=\"elementor-widget-wrap elementor-element-populated\">\n\t\t\t\t\t\t<div class=\"elementor-element elementor-element-8e93283 elementor-widget elementor-widget-text-editor\" data-id=\"8e93283\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t<div class=\"elementor-widget-container\">\n\t\t\t\t\t\t\t\t\t<p>Contact Manager: <a href=\"mailto:desousa@leitat.org\">desousa@leitat.org<\/a><\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t<\/section>\n\t\t\t\t<section class=\"elementor-section elementor-top-section elementor-element elementor-element-cc0cc44 elementor-section-boxed elementor-section-height-default elementor-section-height-default\" data-id=\"cc0cc44\" data-element_type=\"section\" data-e-type=\"section\">\n\t\t\t\t\t\t<div class=\"elementor-container elementor-column-gap-default\">\n\t\t\t\t\t<div class=\"elementor-column elementor-col-50 elementor-top-column elementor-element elementor-element-02316ff\" data-id=\"02316ff\" data-element_type=\"column\" data-e-type=\"column\">\n\t\t\t<div class=\"elementor-widget-wrap elementor-element-populated\">\n\t\t\t\t\t\t<div class=\"elementor-element elementor-element-9e58e0a elementor-widget elementor-widget-image\" data-id=\"9e58e0a\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"image.default\">\n\t\t\t\t<div class=\"elementor-widget-container\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"300\" height=\"200\" src=\"https:\/\/leitat.org\/wp-content\/uploads\/2024\/12\/european-union-logo-300x200-1.png\" class=\"attachment-medium size-medium wp-image-55435\" alt=\"\" \/>\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t<\/div>\n\t\t\t\t<div class=\"elementor-column elementor-col-50 elementor-top-column elementor-element elementor-element-3ccb934\" data-id=\"3ccb934\" data-element_type=\"column\" data-e-type=\"column\">\n\t\t\t<div class=\"elementor-widget-wrap elementor-element-populated\">\n\t\t\t\t\t\t<div class=\"elementor-element elementor-element-20f6470 elementor-widget elementor-widget-text-editor\" data-id=\"20f6470\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t<div class=\"elementor-widget-container\">\n\t\t\t\t\t\t\t\t\tThis project has received funding from the European Union\u2019s Horizon 2020 research and innovation programme under grant agreement No 666918. This publication reflects only the author\u2019s views and the European Union is not liable for any use that may be made of the information contained therein.\n\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t<\/section>\n\t\t\t\t<\/div>\n\t\t","protected":false},"excerpt":{"rendered":"<p>Developing new therapies for Batten disease www.batcure.eu ABSTRACT The goal of BATCure is to advance the development of new therapeutic options for a group of rare lysosomal diseases \u2013 neuronal ceroid lipofuscinoses (NCL) or Batten disease. There are &gt; thousand affected across Europe, with a combined incidence of c.1:100 000. The NCLs are devastating and [&hellip;]<\/p>\n","protected":false},"author":2,"featured_media":55625,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"inline_featured_image":false,"footnotes":""},"categories":[142,120],"tags":[112],"class_list":["post-59840","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-health-technologies-en","category-horizon-2020-en","tag-projects"],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v27.2 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>BATCURE - Leitat Technological Center<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<meta property=\"og:locale\" content=\"en_US\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"BATCURE - Leitat Technological Center\" \/>\n<meta property=\"og:description\" content=\"Developing new therapies for Batten disease www.batcure.eu ABSTRACT The goal of BATCure is to advance the development of new therapeutic options for a group of rare lysosomal diseases \u2013 neuronal ceroid lipofuscinoses (NCL) or Batten disease. 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